Review
Open access
Aug 2026
2026 Update on Clinical Trials in β-Thalassemia.
Several promising approaches targeting fetal hemoglobin induction, iron metabolism, and ineffective erythropoiesis have failed to demonstrate sufficient clinical benefit despite preclinical proof of concept, highlighting the complexity of therapeutic development in β-thalassemia.
K. M. Musallam, F. Locatelli, M. Algeri et al.
· American journal of hematolo... · 0 citations