Sep 2026
Pharmacological inhibitors of the nonsense-mediated RNA decay identified by high-throughput screening.
Three possible candidates acting as NMD inhibitors/modulators that could increase CFTR rescue in patients with PTCs are identified, namely CC-115, samotolisib and elimusertib, and are validated by secondary assays.
Anna Borrelli, Martina de Santis, R. De Cegli et al.
· RNA: A publication of the RN... · 0 citations