Review
Jul 2026
CRISPR-Cas9-based therapies for Huntington’s disease and Friedreich’s ataxia: mechanisms, advances, and future perspectives
Current CRISPR therapeutic strategies for HD and FRDA are examined, including allele-specific editing, transcriptional suppression, repeat excision, epigenetic reactivation, and emerging precision editing approaches such as base editing and prime editing.
Abha Ravikumar Mundada, Amogh Reddy Badikol, Karthik Mangu
· Neurogenetics · 0 citations