Molecular Mechanisms and the Latest Advances in Precision Therapies for Spinal Muscular Atrophy
This review systematically sums up the newest advances in molecular mechanisms and accurate therapies of SMA during the time from 2024 to 2026, which highlights the regulatory roles of SMN1/SMN2 genes, non-coding RNAs, and epigenetic modifications, as well as pathophysiological alterations and disease-modifying factors...