Real-world efficacy and tolerability of lipid-lowering therapy in children with monogenic familial hypercholesterolemia in primary care
Familial hypercholesterolaemia (FH) is characterised by elevated LDL-C levels from an early age and confers a high risk of premature cardiovascular disease. Although guidelines recommend the early initiation of lipid-lowering medication (LLM) following an FH diagnosis, there is limited data on the uptake, effecti...