Review
Open access
Aug 2026
RNA-Based Therapeutics in Genetic Neurodevelopmental Disorders: Bridging Molecular Genetics and Precision Medicine
Overall, continued progress will depend on the integration of disease biology, rational RNA therapeutic design, and effective CNS-targeted delivery, supporting the broader implementation of precision RNA medicine for genetic neurodevelopmental disorders.
I. Focșa, C. Iliescu, C. Pomeran et al.
· International Journal of Mol... · 0 citations