Review
Open access
Jul 2026
Management of patients with rare diseases in the Middle East: challenges & opportunities – insights from the Rare Advocacy Council
Key challenges identified included the lack of national disease registries, limited public awareness, underrepresentation of patient voices in decision-making, fragmented multidisciplinary care, and restricted access to diagnostics and advanced therapies.
A. Farrugia, A. Bahey, A. Tarawah et al.
· Orphanet Journal of Rare Dis... · 0 citations