Review
Aug 2026
Gene therapy clinical trials for inherited eye diseases: The pediatric perspective.
While the field of pediatric ophthalmology shows promise for gene therapy options, future strategies should include stratified enrollment based on age, separate cohorts for pediatric and adult patients, or adaptive trial designs.
A. Sandali, Anna Nikolaidou, Theodora Gianni et al.
· European Journal of Ophthalm... · 0 citations