N. Goriot-Raynaud

Peripheral muscle dysfunction persists in the era of highly effective CFTR modulators in cystic fibrosis.

BACKGROUND Peripheral muscle dysfunction is a well-established extrapulmonary manifestation of cystic fibrosis (CF), contributing to exercise intolerance and reduced quality of life. However, its persistence in the era of highly effective CFTR modulator therapy (HEMT) remains unclear. METHODS Fifty-six people with CF...