Review
Open access
Aug 2026
Progressive familial intrahepatic cholestasis disease burden and clinical approaches: a systematic review.
Current evidence supports improvements in pruritus and serum bile acid control, particularly in PFIC2/BSEP deficiency; however, treatment responses are heterogeneous and additional long-term clinical and economic evidence is needed.
S. Horslen, G. Vogel, Jolan Terner-Rosenthal et al.
· Journal of Comparative Effec... · 1 citation