Factor IX Padua AAV gene therapy in adolescents with hemophilia B: a phase 1 trial.
F. Xue
Ai Zhang
Mankai Ju
Xia Wu
Bing-Qi Xu
Xiao-Lei Pei
Yu-Hua Wang
Wei Liu
Ai-Guo Liu
Wei Jiang
Xin-Yue Dai
Yunfei Chen
Xiao-Fan Liu
Rong-Feng Fu
Ting Sun
Wen-Jing Gu
Jing Zheng
Zeng-Ming Du
Cai-Xia Yang
Xiao Xiao
Ren-Chi Yang
Qun Hu
Lei Zhang
Medicine