Intraputaminal AAV9 co-delivery of AADC and GDNF in severe AADC deficiency: first-in-human pediatric dose-escalation study.
Feng Han
Ping-Ping Gao
You-Feng Zhou
T. Cui
Yi-Chao Xu
Xi Fang
Min Shen
Su-Zhen Dong
Yu-Min Zhong
Ying-Yan Wang
Li-Jun Bu
Li Chen
Yuan-Yi Xia
Ru-En Yao
Nan Bao
Bin Xue
Ying-Ying Tao
Jing-Jie Ge
Z. Ju
Yu-Hua Zhu
Y. Guan
Chuan-Tao Zuo
Xin-Yan Sun
Shan-Xiong Ding
Gui-Zhang Cao
Xian-Feng Wang
Li Feng
Hong-Xia Mao
Hua Lv
Xiao-Ping Zhao
Wei Li
Ji-Wen Wang
Yun-Hai Song
Medicine