Open access
Functional validation of allele-specific LMNB1 silencing in patient-derived astrocytes as a therapeutic option for Autosomal Dominant Leukodystrophy
Martina Lorenzati
Arianna Contato
F. Josa-Prado
Marta Ribodino
M. K. Ardakani
Ersilia Nicorvo
Elena Signorino
G. Turrini
V. Cerrato
Roberta Parolisi
F. Lucchini
G. Piacenti
Giacomo Donati
V. Proserpio
J. García-León
Marzia Rossato
Luciano Conti
A. Brusco
G. Ramazzotti
Stefano Ratti
Pietro Cortelli
Elisa Giorgio
A. Buffo
Biology