Precision Medicine in Sickle Cell Disease: From Molecular Pathways to Curative Strategies.
Sickle cell disease (SCD) is a monogenic β-globin disorder characterized by hemoglobin S polymerization, hemolysis, and vaso-occlusion, yet it exhibits remarkable clinical heterogeneity. Despite advances in supportive care and disease-modifying therapies, substantial variability in severity, treatment response, and lon...
Dina Tluli, Omar Tluli, Abdelrahman A. Karen et al.
· Hemoglobin · 0 citations