Patient perspectives on gene therapies and gene editing for familial cardiomyopathies
Gene replacement and gene editing therapies for cardiomyopathies are in early-phase clinical trials. However, limited data exist on patient perspectives. We assessed adult familial cardiomyopathy patient perspectives towards the clinical implementation of somatic genetic therapies. Patients completed a demographic surv...
Anjali Narain, Kayla Ruiz, Matthew T. Wheeler et al.
· BMC Medical Genomics · 0 citations