Advancements in CRISPR-based in vivo gene therapy for hemophilia
Recent advances and feasible strategies of CRISPR/Cas9-based genome editing for hemophilia therapy are outlined, the potential applications of next-generation gene editing and vector delivery technologies are highlighted, and new insights are offered for the advantages, limitations, and future directions for these nove...
Xiao-Yu Zhang, Kai-Di Xu, Shi-Hui Zou et al.
· Frontiers in Genome Editing · 0 citations