Lipid nanoparticles optimized for large RNA cargo and tissue targeting enhance in vivo genome editing.
Song-Tao Dong
Fang-Lin Gong
Tyler Thomson
Yun-Shu Cai
Lauren Healy
R. X. Z. Lu
Zi-Yu Zhou
Yue Xu
Jin-Gan Chen
Margarita Savguira
Xiang-Lei Fu
Sijin Luozhong
Mu-Ye Zhou
Payton J. Kirtley
Brandon K. Wilder
Bo-Wen Li
Medicine