Open access
LNP-mediated BCL11A Editing Corrects Sickling Phenotypes and Preserves HSPC Fitness Compared to Electroporation
Y. Ansong-Ansongton
C. S. A. Adanho
Utku Goreke
A. Lawanprasert
M. Vysotskiy
York Tang
Alissa LW Kleinhez
Ross C. Wilson
Angela Rivers
N. Murthy
David N. Nguyen
Biology